medical research

Health
2:43 am
Mon December 22, 2014

A Family's Long Search For Fragile X Drug Finds Frustration, Hope

Katie Clapp shares a laugh with her son Andy Tranfaglia, 25, at their home in West Newbury, Mass. Andy has a rare genetic condition called fragile X syndrome.
Ellen Webber for NPR

Originally published on Tue December 23, 2014 1:22 pm

For a few weeks last year, Michael Tranfaglia and Katie Clapp saw a remarkable change in their son, Andy, who'd been left autistic and intellectually disabled by fragile X syndrome. Andy, who is 25, became more social, more talkative and happier. "He was just doing incredibly well," his father says.

Read more
Health
3:19 pm
Tue September 16, 2014

Breast Cancer Patients Seek More Control Over Research Agenda

Coalitions of patient advocates now help steer research funding toward particular projects.
Lilli Carré for NPR

Originally published on Tue September 23, 2014 10:23 am

The federal government has poured more than $3 billion into breast cancer research over the past couple of decades, but the results have been disappointing. The disease remains a stubborn killer of women.

So the National Breast Cancer Coalition is trying something bold: The advocacy group has decided that it's not simply going to lobby for more research dollars. Instead, its leaders are sitting down at the table with scientists studying the disease and telling them how they'd like that money to be spent.

Read more
Health
4:23 pm
Thu August 14, 2014

Heads Still Dry, Scientists Try New Approach With ALS

Houston Texans Coach Bill O'Brien (center) Chief Operating Officer Cal McNair (right) and Houston Chronicle reporter Brian Smith take the ALS Ice Bucket Challenge Thursday to raise money for the ALS Association.
David J. Phillip AP

Originally published on Mon August 18, 2014 6:49 am

While your Facebook friends douse themselves with buckets of ice-cold water to raise money to fight amyotrophic lateral sclerosis, an international team of scientists said they'd taken a small step toward drowning out the deadly disease.

Researchers from the Scripps Research Institute and the Mayo Clinic developed a new drug that combats molecular contributors to ALS, which currently afflicts more than 30,000 Americans.

Read more
Science and Environment
2:44 am
Tue April 8, 2014

How Mouse Studies Lead Medical Research Down Dead Ends

I'm not trying to lead you astray. It's just that scientists are not skeptical enough about their mouse studies.
iStockphoto

Originally published on Wed April 9, 2014 7:59 am

Most experimental drugs fail before they make it through all the tests required to figure out if they actually work and if they're safe. But some drugs get fairly far down that road, at the cost of hundreds of millions of dollars, based on poorly conducted studies at the outset.

Medical researchers reviewing this sorry state of affairs say the drug-development process needs serious improvement.

Read more